TY - JOUR
AU - Gronostay, Alexandra
AU - Jost, Stefanie Theresa
AU - Silverdale, Monty
AU - Rizos, Alexandra
AU - Loehrer, Philipp Alexander
AU - Evans, Julian
AU - Sauerbier, Anna
AU - Indi, Donya
AU - Leta, Valentina
AU - Reker, Paul
AU - Fink, Gereon Rudolf
AU - Ashkan, Keyoumars
AU - Antonini, Angelo
AU - Nimsky, Christopher
AU - Visser-Vandewalle, Veerle
AU - Martinez-Martin, Pablo
AU - Ray Chaudhuri, K.
AU - Timmermann, Lars
AU - Dafsari, Haidar S
TI - Stratifying quality of life outcome in subthalamic stimulation for Parkinson’s disease
JO - Journal of neurology, neurosurgery, and psychiatry
VL - 95
IS - 7
SN - 0022-3050
CY - London
PB - BMJ Publishing Group
M1 - FZJ-2024-02262
SP - jnnp-2023-332272 -
PY - 2024
N1 - Paper is funded by the German Research Foundation (Grant KFO 219)
AB - ABSTRACTBackground Subthalamic nucleus deep brainstimulation (STN-DBS)for Parkinson’s disease (PD)improves quality of life (QoL), motor and non-motorsymptoms (NMS). However, in previous studies, 43%–49% of patients did not experience clinically relevantpostoperative QoL improvement. To inform individualisedprediction of postoperative QoL improvement, wedeveloped a stratification analysis of QoL outcomesbased on preoperative non-motortotal burden, severityof motor progression and motor response in levodopachallenge tests.Methods This was a prospective, open-label,multicentre, international study with a 6-monthfollow-up.A distribution-basedthreshold identified’QoL responders’ in the PDQuestionnaire-8SummaryIndex (PDQ-8SI). After baseline stratification based onthe NMS Scale, Hoehn and Yahr Scale and levodoparesponse assessed with the Unified PD Rating Scale-III,we compared postoperative QoL response between thesestrata. To assess the clinical usefulness and statisticalfeasibility of stratifications, we compared cumulativedistribution function curves, respectively PDQ-8within-stratumvariation.Results All main outcomes improved postoperatively.Based on the 8.1 points threshold for clinicallymeaningful PDQ-8SI improvement, only 80/161 patientswere classified as ’QoL responders’. The absolute riskreductions for QoL non-responseamong respective non-motor,motor progression and levodopa response stratawere 23%, 8% and 3%, respectively. Only non-motorstratification reduced PDQ-8within-stratumvariationcompared with the overall cohort.Conclusions Non-motorstratification, but not motorprogression or levodopa response stratification, isclinically useful and statistically feasible for personalisedpreoperative prediction of postoperative QoL outcome ofSTN-DBSfor PD. Our findings highlight that non-motorassessments are necessary components of a case-based,holistic approach of DBS indication evaluations gearedtowards optimising postoperative QoL outcomes.
LB - PUB:(DE-HGF)16
C6 - 38124227
UR - <Go to ISI:>//WOS:001143623900001
DO - DOI:10.1136/jnnp-2023-332272
UR - https://juser.fz-juelich.de/record/1024588
ER -