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@ARTICLE{Konitsioti:1037240,
author = {Konitsioti, Agni M. and Prüss, Harald and Laurent, Sarah
and Fink, Gereon Rudolf and Heesen, Christoph and Warnke,
Clemens},
title = {{C}himeric antigen receptor {T}-cell therapy for autoimmune
diseases of the central nervous system: a systematic
literature review},
journal = {Journal of neurology},
volume = {271},
number = {10},
issn = {0367-004X},
address = {[Darmstadt]},
publisher = {Steinkopff},
reportid = {FZJ-2025-00573},
pages = {6526 - 6542},
year = {2024},
note = {Funding Open Access funding enabled and organized by
Projekt DEAL.},
abstract = {Importance: B-cell-targeting monoclonal antibodies have
demonstrated safety and efficacy in multiple sclerosis or
anti-aquaporin-4 IgG positive neuromyelitis optica spectrum
disorder. However, these therapies do not facilitate
drug-free remission, which may become possible with
cell-based therapies, including chimeric antigen receptor
(CAR) T cells. CAR T-cell therapy holds promise for
addressing other antibody-mediated CNS disorders, e.g.,
MOG-associated disease or autoimmune encephalitis.Objective:
To provide an overview of the current clinical knowledge on
CAR T-cell therapy in central nervous system
autoimmunity.Evidence review: We searched PubMed, Embase,
Google Scholar, PsycINFO, and clinicaltrials.gov using the
terms 'CAR T cell' and 'multiple sclerosis/MS' or
'neuromyelitis optica/spectrum diseases/NMOSD' or
'MOG-associated disease/MOGAD 'or' autoimmune encephalitis'
or 'neuroimmunology'.Findings: An ongoing phase I clinical
trial has indicated the safety and benefits of anti-BCMA CAR
T cells in 12 patients with AQP4-IgG seropositive
neuromyelitis optica spectrum disorder. Case reports
involving two individuals with progressive multiple
sclerosis and one patient with stiff-person syndrome
demonstrated a manageable safety profile following treatment
with anti-CD19 CAR T cells. Recruitment has commenced for
two larger studies in MS, and a phase I open-label basket
study is underway to evaluate BCMA-directed CAR T cells in
various antibody-associated inflammatory diseases, including
MOG-associated disease. Preclinical research on NMDA
receptor antibody autoimmune encephalitis treated with
chimeric autoantibody receptor T cells generated promising
data.Conclusions and relevance: There is minimal evidence of
the benefits of CAR T-cell therapy in individuals with
central nervous system-directed autoimmunity. Nevertheless,
multicenter controlled clinical trials with a manageable
safety profile appear feasible and are warranted due to very
promising case experiences.Keywords: Antibody-mediated CNS
disorders; CAR T-cell therapy; Central nervous system
autoimmunity; Multiple sclerosis; NMOSD.},
cin = {INM-3},
ddc = {610},
cid = {I:(DE-Juel1)INM-3-20090406},
pnm = {5251 - Multilevel Brain Organization and Variability
(POF4-525)},
pid = {G:(DE-HGF)POF4-5251},
typ = {PUB:(DE-HGF)16},
pubmed = {39276207},
UT = {WOS:001321346700002},
doi = {10.1007/s00415-024-12642-4},
url = {https://juser.fz-juelich.de/record/1037240},
}