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@ARTICLE{Schuler:839969,
author = {Schuler, Nadine and Palm, Jan and Schmitz, Sabine and
Lorat, Yvonne and Rübe, Claudia E.},
title = {{I}ncreasing genomic instability during cancer therapy in a
patient with {L}i-{F}raumeni syndrome},
journal = {Clinical and translational radiation oncology},
volume = {7},
issn = {2405-6308},
address = {Amsterdam},
publisher = {Elsevier},
reportid = {FZJ-2017-07543},
pages = {71 - 78},
year = {2017},
abstract = {Background: Li-Fraumeni syndrome (LFS) is a cancer
predisposition disorder characterized by germlinemutations
of the p53 tumor-suppressor gene. In response to DNA damage,
p53 stimulates protective cellularprocesses including
cell-cycle arrest and apoptosis to prevent aberrant cell
proliferation. Currentcancer therapies involve agents that
damage DNA, which also affect non-cancerous
hematopoieticstem/progenitor cells. Here, we report on a
child with LFS who developed genomic instability
duringcraniospinal irradiation for metastatic choroid plexus
carcinoma (CPC).Case presentation: This previously healthy
4-year-old boy presented with parieto-temporal brain
tumor,diagnosed as CPC grade-3. Screening for
cancer-predisposing syndrome revealed heterozygous p53
germlinemutation, leading to LFS diagnosis. After tumour
resection and systemic chemotherapy, entire craniospinalaxis
was irradiated due to leptomeningeal seeding, resulting in
disease stabilization for nearly12 months. Blood lymphocytes
of LFS patient (p53-deficient) and age-matched
tumor-children (p53-proficient) were collected before,
during and after craniospinal irradiation and compared with
asymptomaticcarriers for identical p53 mutation, not exposed
to DNA-damaging treatment. In p53-deficientlymphocytes of
LFS patient radiation-induced DNA damage failed to induce
cell-cycle arrest or apoptosis.Although DNA repair capacity
was not impaired, p53-deficient blood lymphocytes of LFS
patient showedsignificant accumulation of 53BP1-foci during
and even several months after irradiation, reflecting
persistentDNA damage. Electron microscopy revealed DNA
abnormalities ranging from simple unrepairedlesions to
chromosomal abnormalities. Metaphase spreads of
p53-deficient lymphocytes explored bymFISH revealed high
amounts of complex chromosomal aberrations after
craniospinal irradiation.Conclusions: Tumor suppressor p53
plays a central role in maintaining genomic stability by
promotingcell-cycle checkpoints and apoptosis. Here, we
demonstrate that a patient with LFS receiving
craniospinalirradiation including large volumes of bone
marrow developed progressive genomic instability of
thehematopoietic system. During DNA-damaging radiotherapy,
genome-stabilizing mechanisms in
proliferatingstem/progenitor cells are perturbed by p53
deficiency, increasing the risk of cancer initiation
andprogression.},
cin = {S-US},
ddc = {610},
cid = {I:(DE-Juel1)S-US-20090406},
pnm = {899 - ohne Topic (POF3-899)},
pid = {G:(DE-HGF)POF3-899},
typ = {PUB:(DE-HGF)16},
pubmed = {pmid:29594232},
UT = {WOS:000458475000011},
doi = {10.1016/j.ctro.2017.10.004},
url = {https://juser.fz-juelich.de/record/839969},
}