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@ARTICLE{Elfgen:889730,
author = {Elfgen, Anne and Santiago-Schübel, Beatrix and Hupert,
Michelle and Schemmert, Sarah and Schartmann, Elena and
Tusche, Markus and Gering, Ian and Zafiu, Christian and
Kutzsche, Janine},
title = {{O}ral absorption enhancement of the amyloid-β oligomer
eliminating compound {RD}2 by conjugation with folic acid},
journal = {European journal of pharmaceutical sciences},
volume = {156},
issn = {0928-0987},
address = {New York, NY [u.a.]},
publisher = {Elsevier},
reportid = {FZJ-2021-00351},
pages = {105581 -},
year = {2021},
abstract = {Amyloid-β (Aβ) plays a central role in the development
and progression of Alzheimer's disease (AD) with Aβ
oligomers representing the most toxic species. The
all-d-enantiomeric peptide RD2, which recently successfully
completed clinical phase I, specifically eliminates Aβ
oligomers in vitro as well as in vivo and improves cognitive
deficits in various transgenic AD mouse models even after
oral administration. To further enhance the oral absorption
of RD2, folic acid has been conjugated to the d-peptide
promoting an endocytosis-mediated uptake via a folate
receptor located in the intestine. Two different conjugation
strategies were selected to obtain prodrugs with folic acid
being cleaved after intestinal absorption releasing
unmodified RD2 in order to enable RD2's unaltered systemic
efficacy. Both conjugates remained stable in simulated
gastrointestinal fluids. But only one of them was suitable
as prodrug as it was cleaved to RD2 in vitro in human blood
plasma and liver microsomes and in vivo in mice after
intravenous injection leading to a systemic release of RD2.
Furthermore, the conjugate's permeability in vitro and after
oral administration in mice was strongly enhanced compared
to unconjugated RD2 demonstrating the prodrug's
functionality. However, the conjugate seemed to have
impaired the mice's wellbeing shortly after oral
administration possibly resulting from strain-specific
hypersensitivity to folic acid. Nevertheless, we assume that
the prodrug is actually non-toxic, especially in lower
concentrations as verified by a cell viability test.
Furthermore, lower dosages can be applied with unaltered
efficacy due to its enhanced oral absorption.},
cin = {IBI-7 / ZEA-3},
ddc = {610},
cid = {I:(DE-Juel1)IBI-7-20200312 / I:(DE-Juel1)ZEA-3-20090406},
pnm = {5244 - Information Processing in Neuronal Networks
(POF4-524)},
pid = {G:(DE-HGF)POF4-5244},
typ = {PUB:(DE-HGF)16},
pubmed = {33035662},
UT = {WOS:000597224100001},
doi = {10.1016/j.ejps.2020.105581},
url = {https://juser.fz-juelich.de/record/889730},
}