% IMPORTANT: The following is UTF-8 encoded. This means that in the presence % of non-ASCII characters, it will not work with BibTeX 0.99 or older. % Instead, you should use an up-to-date BibTeX implementation like “bibtex8” or % “biber”. @ARTICLE{PetrySchmelzer:892509, author = {Petry-Schmelzer, Jan Niklas and Keller, Natalie and Karakaya, Mert and Wirth, Brunhilde and Fink, Gereon R. and Wunderlich, Gilbert}, title = {{VPS}13{D} : {O}ne {F}amily, {S}ame {M}utations, {T}wo {P}henotypes}, journal = {Movement disorders clinical practice}, volume = {8}, number = {5}, issn = {2330-1619}, address = {New York, NY}, publisher = {Wiley}, reportid = {FZJ-2021-02118}, pages = {803-806}, year = {2021}, abstract = {Here, we report two siblings with compound heterozygous variants in VPS13D but a considerable divergent phenotype highlighting the difficulties of phenotype–genotype correlation in this rare disease.A 19-year-old patient presented to our outpatient department with a five-year history of progressive gait impairment. Motor and cognitive development during childhood was described as normal. The patient visited a regular school and was able to participate in physical education until the onset of symptoms. There were no known neurologic diseases in the Caucasian family, consisting of five sisters (II.1–3, II.5, and II.6), and the patient (II.4). However, one younger sister (II.6) of the patient suffered from developmental delay and intellectual disability without further physical impairment, and the oldest sister (II.1) living separate from the family was supposed to have “gait problems”.}, cin = {INM-3}, ddc = {610}, cid = {I:(DE-Juel1)INM-3-20090406}, pnm = {525 - Decoding Brain Organization and Dysfunction (POF4-525)}, pid = {G:(DE-HGF)POF4-525}, typ = {PUB:(DE-HGF)16}, pubmed = {pmid:34307758}, UT = {WOS:000647076200001}, doi = {10.1002/mdc3.13232}, url = {https://juser.fz-juelich.de/record/892509}, }