% IMPORTANT: The following is UTF-8 encoded. This means that in the presence
% of non-ASCII characters, it will not work with BibTeX 0.99 or older.
% Instead, you should use an up-to-date BibTeX implementation like “bibtex8” or
% “biber”.
@ARTICLE{Pagano:909580,
author = {Pagano, Gennaro and Taylor, Kirsten I. and Anzures-Cabrera,
Judith and Marchesi, Maddalena and Simuni, Tanya and Marek,
Kenneth and Postuma, Ronald B. and Pavese, Nicola and
Stocchi, Fabrizio and Azulay, Jean-Philippe and Mollenhauer,
Brit and López-Manzanares, Lydia and Russell, David S. and
Boyd, James T. and Nicholas, Anthony P. and Luquin, María
R. and Hauser, Robert A. and Gasser, Thomas and Poewe,
Werner and Ricci, Benedicte and Boulay, Anne and Vogt,
Annamarie and Boess, Frank G. and Dukart, Jürgen and
D’Urso, Giulia and Finch, Rebecca and Zanigni, Stefano and
Monnet, Annabelle and Pross, Nathalie and Hahn, Andrea and
Svoboda, Hanno and Britschgi, Markus and Lipsmeier, Florian
and Volkova-Volkmar, Ekaterina and Lindemann, Michael and
Dziadek, Sebastian and Holiga, Štefan and Rukina, Daria and
Kustermann, Thomas and Kerchner, Geoffrey A. and Fontoura,
Paulo and Umbricht, Daniel and Doody, Rachelle and
Nikolcheva, Tania and Bonni, Azad},
title = {{T}rial of {P}rasinezumab in {E}arly-{S}tage
{P}arkinson’s {D}isease},
journal = {The New England journal of medicine},
volume = {387},
number = {5},
issn = {0028-4793},
address = {Waltham, Mass.},
publisher = {MMS},
reportid = {FZJ-2022-03262},
pages = {421 - 432},
year = {2022},
abstract = {Background: Aggregated α-synuclein plays an important role
in the pathogenesis of Parkinson's disease. The monoclonal
antibody prasinezumab, directed at aggregated α-synuclein,
is being studied for its effect on Parkinson's
disease.Methods: In this phase 2 trial, we randomly assigned
participants with early-stage Parkinson's disease in a 1:1:1
ratio to receive intravenous placebo or prasinezumab at a
dose of 1500 mg or 4500 mg every 4 weeks for 52 weeks. The
primary end point was the change from baseline to week 52 in
the sum of scores on parts I, II, and III of the Movement
Disorder Society-sponsored revision of the Unified
Parkinson's Disease Rating Scale (MDS-UPDRS; range, 0 to
236, with higher scores indicating greater impairment).
Secondary end points included the dopamine transporter
levels in the putamen of the hemisphere ipsilateral to the
clinically more affected side of the body, as measured by
123I-ioflupane single-photon-emission computed tomography
(SPECT).Results: A total of 316 participants were enrolled;
105 were assigned to receive placebo, 105 to receive 1500 mg
of prasinezumab, and 106 to receive 4500 mg of prasinezumab.
The baseline mean MDS-UPDRS scores were 32.0 in the placebo
group, 31.5 in the 1500-mg group, and 30.8 in the 4500-mg
group, and mean (±SE) changes from baseline to 52 weeks
were 9.4±1.2 in the placebo group, 7.4±1.2 in the 1500-mg
group (difference vs. placebo, -2.0; $80\%$ confidence
interval [CI], -4.2 to 0.2; P = 0.24), and 8.8±1.2 in the
4500-mg group (difference vs. placebo, -0.6; $80\%$ CI, -2.8
to 1.6; P = 0.72). There was no substantial difference
between the active-treatment groups and the placebo group in
dopamine transporter levels on SPECT. The results for most
clinical secondary end points were similar in the
active-treatment groups and the placebo group. Serious
adverse events occurred in $6.7\%$ of the participants in
the 1500-mg group and in $7.5\%$ of those in the 4500-mg
group; infusion reactions occurred in $19.0\%$ and $34.0\%,$
respectively.Conclusions: Prasinezumab therapy had no
meaningful effect on global or imaging measures of
Parkinson's disease progression as compared with placebo and
was associated with infusion reactions. (Funded by F.
Hoffmann-La Roche and Prothena Biosciences; PASADENA
ClinicalTrials.gov number, NCT03100149.).},
cin = {INM-7},
ddc = {610},
cid = {I:(DE-Juel1)INM-7-20090406},
pnm = {5251 - Multilevel Brain Organization and Variability
(POF4-525) / 5253 - Neuroimaging (POF4-525)},
pid = {G:(DE-HGF)POF4-5251 / G:(DE-HGF)POF4-5253},
typ = {PUB:(DE-HGF)16},
pubmed = {35921451},
UT = {WOS:000861612100008},
doi = {10.1056/NEJMoa2202867},
url = {https://juser.fz-juelich.de/record/909580},
}